Elevidys

DNA gene therapy gene editing helix CRISPR

Regenxbio starts pivotal study for DMD gene therapy

Regenxbio’s gene therapy improved muscle function for patients with DMD in a phase 1/2 study, with the biotech rolling the trial into a pivotal study.

Gabrielle Masson Nov 18, 2024 2:24pm

Sarepta's next DMD drug seems to get the job done in phase 2

Jan 29, 2024 10:49am