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spinal muscular atrophy
Biotech
Phase 3 Scholar Rock trial hits SMA goal, sending stock up 327%
Investors went wild despite the higher dose falling short of the targeted efficacy and Scholar Rock making no mention of a key secondary goal.
Nick Paul Taylor
Oct 7, 2024 8:45am
Roche, Abu Dhabi partner to study rare spinal disease
May 23, 2024 5:30am
Novartis, Voyager launch $100M gene therapy mission
Jan 2, 2024 8:31am
David Liu's lab finds base editing may spur one-time SMA therapy
Mar 31, 2023 2:46pm
Celgene, Acceleron alum Backstrom tapped to lead Scholar Rock
Sep 20, 2022 11:20am
Scholar Rock bags $205M as 24-month data point to SMA durability
Jun 17, 2022 10:34am
